Meaning of retinoblastoma: A childhood eye cancer usually noticed as a white glow in the pupil, and the tumor that revealed how cancer genes work.

Definition of retinoblastoma

Retinoblastoma is a cancer that arises in the retina, the light-sensing layer at the back of the eye. It almost always occurs in young children, before school age. It develops when both copies of the RB1 gene are lost or damaged in a developing retinal cell. Some children inherit one faulty copy, in which case tumors tend to appear earlier and in both eyes.

How is it usually noticed?

The most common first sign is leukocoria, a white reflection from the pupil where the red reflex should be. It is often spotted in a photograph taken with a flash, or by a parent in dim light. The second common sign is a squint, where the eyes do not point in the same direction, because a tumor blocking central vision removes the reason for that eye to align. Pain is unusual early on, and a young child cannot report reduced vision in one eye, so the outward signs matter.

What is the difference between the inherited and non-inherited forms?

Heritable formNon-heritable form
First faulty gene copyPresent in every cell from birthArises in one retinal cell
Eyes affectedOften bothOne
Number of tumorsFrequently severalUsually one
Age at diagnosisEarlierLater
Other cancers laterRaised riskNot raised

Why is this tumor important beyond the eye?

Retinoblastoma is where the idea of a tumor suppressor gene came from. RB1 normally acts as a brake on cell division. One working copy is enough, so a cell only loses control when both copies fail. A child with a hereditary fault already carries one broken copy in every cell of the body, so a single further event in any retinal cell is enough, which explains why tumors appear early and in more than one place. This two-step model now underpins how many other inherited cancer risks are understood. Children with the heritable form also carry a raised lifetime risk of other cancers, particularly bone tumors, which is why follow-up continues long after the retina is treated.

Used in a sentence

Examination under anesthesia confirmed bilateral retinoblastoma.

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Good to know

A white pupil reflex in a young child is the classic presenting sign, and children with the heritable form carry a raised risk of separate cancers later in life.

Word origin

Where “retinoblastoma” comes from

Joins the Latin rete, meaning net, which gives retina, with the Greek blastos, a germ or sprout, and -oma, a tumor.

For learning, not diagnosis. This glossary provides general educational information and is not a substitute for advice from a qualified healthcare professional. If you may be experiencing a medical emergency, contact local emergency services.